Celebrating Rare Disease Day with Jett Foundation

Friday, February 26, 2021 | 2:00-3:30 PM ET

Support Local Artist Living with DMD

We invite you to support one of our patients with his fundraiser campaign.

RDR Investigator-Sponsored Trial Treats First Patient

We announce the enrollment of the first patient in our Investigator-Sponsored Trial for boys with Duchenne muscular dystrophy.