Support Local Artist Living with DMD
We invite you to support one of our patients with his fundraiser campaign.
RDR Investigator-Sponsored Trial Treats First Patient
We announce the enrollment of the first patient in our Investigator-Sponsored Trial for boys with Duchenne muscular dystrophy.
Clinical study for the treatment of Dravet Syndrome
Clinical study for the treatment of Dravet Syndrome available at Rare Disease Research
Clinical Study for the treatment of Dyskinesia in Cerebral Palsy (DCP)
Clinical study for the treatment of Dyskinesia in Cerebral Palsy available at Rare Disease Research.
Clinical Study for patients with Metachromatic Leukodystrophy (MLD)
Clinical Study for patients with Tourette Syndrome available at Rare Disease Research.