We announce the enrollment of the first patient in our Investigator-Sponsored Trial for boys with Duchenne muscular dystrophy.

Clinical study for the treatment of Dravet Syndrome available at Rare Disease Research

Clinical study for the treatment of Dyskinesia in Cerebral Palsy available at Rare Disease Research.

Clinical Study for patients with Tourette Syndrome available at Rare Disease Research.

Clinical Study for patients with Tourette Syndrome available at Rare Disease Research.

Clinical Study for patients with Myasthenia Gravis available at Rare Disease Research.

Make your gift today so that PPMD can maintain their commitment to research, care, and advocacy in the face of the most challenging time we’ve ever experienced.

In the words of one of our patients, Ethan LyBrand, "Through the good times and bad, the Muscular Dystrophy Association helps kids like me."

RDR is closely monitoring the ongoing Coronavirus disease pandemic (2019).  As the current situation continues to change, our utmost priority is the health and safety of RDR staff, patients, and their families.