RDR Investigator-Sponsored Trial Treats First Patient

We announce the enrollment of the first patient in our Investigator-Sponsored Trial for boys with Duchenne muscular dystrophy.


Clinical study for the treatment of Dravet Syndrome

Clinical study for the treatment of Dravet Syndrome available at Rare Disease Research


Clinical Study for the treatment of Dyskinesia in Cerebral Palsy (DCP)

Clinical study for the treatment of Dyskinesia in Cerebral Palsy available at Rare Disease Research.


Clinical Study for patients with Metachromatic Leukodystrophy (MLD)

Clinical Study for patients with Tourette Syndrome available at Rare Disease Research.


Clinical Study for patients with Tourette Syndrome

Clinical Study for patients with Tourette Syndrome available at Rare Disease Research.


Clinical Study for patients with Myasthenia Gravis

Clinical Study for patients with Myasthenia Gravis available at Rare Disease Research.